Topic-Contributed Paper Session
Advances in Statistical Methods for ALS and Other Rare Disease Clinical Trials: Joint Models, Patient-Prioritized Outcomes, and Hybrid External Controls
Biopharmaceutical Section co: No Additional Sponsorco: No Additional Sponsor Applied
4 Presentations
8:35 AM - 8:55 AM
Matteo Vestrucci (Berry Consultants)
8:55 AM - 9:15 AM
Arlina Shen (Stanford University)
9:15 AM - 9:35 AM
9:35 AM - 9:55 AM
Austin Hand (Corcept Therapeutics)
Discussant
Ying Lu (Stanford University School of Medicine)