Online Program

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Friday, September 14
Fri, Sep 14, 11:15 AM - 12:30 PM
Lincoln 5
Innovations in Rare Disease Clinical Programs

Combining Clinical Progression Modeling with Innovative Trial Design in Rare Disease Trials (300744)

Scott Berry, Berry Consultants 
*Melanie Quintana, Berry Consultants 

Keywords: Clinical progression modeling, Adaptive Trials, Bayesian

In this talk I will present the use of clinical progression modeling in rare diseases and the statistical and clinical value of these models in clinical trials. The clinical progression models can be combined with innovative trial designs, including adaptive and platform trials to create additional statistical synergy. Several examples will be presented.