Online Program Home
My Program

Keyword Search

Legend:
CC = Vancouver Convention Centre   F = Fairmont Waterfront Vancouver
* = applied session       ! = JSM meeting theme

Keyword Search Criteria: rare diseases returned 5 record(s)
Sunday, 07/29/2018
Advancing Methodologies for Clinical Trials Using Historical Control
Min Min, U.S. Food and Drug Administration, CDER/OTS/OB; Yeh-Fong Chen, US FDA
2:45 PM

Monday, 07/30/2018
A Generalized Design for a Confirmatory Basket Trial
Robert Beckman, Georgetown University; Xiaoyun (Nicole) Li, Merck
2:25 PM

Wednesday, 08/01/2018
On Randomized Controlled Trials with Integrated Real World Evidence for Drug Development in Rare Diseases
Qing Liu, Amicus Therapeutics, Inc
11:15 AM

Bayes in Drug Development for Rare Diseases
John Scott, FDA
11:35 AM

Thursday, 08/02/2018
Statistical Challenges and Opportunities in Drug Development for Rare Diseases
Guowen Sun, BioMarin; Keith Gregg, BioMarin; Peter Slasor, BioMarin; Chito Hernandez, BioMarin Pharmaceutical Inc.
9:50 AM